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New drug approvals and regulatory decisions from the FDA. Includes NDA approvals, breakthrough therapy designations, and complete response letters.

LATEST EVENTS
Entity Type Summary Impact Confidence
roflumilast cream regulatory Upcoming FDA decision for roflumilast cream for pediatric plaque psoriasis expected in Q2 2026. medium 95%
baxdrostat regulatory Upcoming FDA decision for baxdrostat for hypertension expected in Q2 2026. medium 95%
olezarsen regulatory Upcoming FDA decision for olezarsen for severe hypertriglyceridemia expected in Q2 2026. medium 95%
cytisinicline regulatory Upcoming FDA decision for cytisinicline for smoking cessation expected in Q2 2026. medium 95%
inhaled insulin regulatory Upcoming FDA decision for inhaled insulin for pediatric patients expected in Q2 2026. medium 95%
sparsentan regulatory Upcoming FDA decision for sparsentan in focal segmental glomerulosclerosis expected in Q2 2026. medium 95%
Praxis Precision Medicines regulatory Praxis Precision Medicines announced FDA acceptance and priority review of NDA for relutrigine for SCN2A and SCN8A DEEs. high 98%
Egetis Therapeutics regulatory Egetis Therapeutics announced FDA acceptance and priority review of NDA for Emcitate (tiratricol) for MCT8 deficiency. high 98%
RP1 regulatory Upcoming FDA complete response letter for RP1 in advanced melanoma expected in Q2 2026. medium 95%
trastuzumab deruxtecan regulatory Upcoming FDA decision on sBLA for trastuzumab deruxtecan in HER2-positive early breast cancer expected in Q2 2026. medium 95%
vepdegestrant regulatory Upcoming FDA decision on NDA for vepdegestrant for ESR1-mutant breast cancer expected in Q2 2026. medium 95%
sonrotoclax regulatory Upcoming FDA decision on NDA for sonrotoclax in relapsed/refractory mantle cell lymphoma expected in Q2 2026. medium 95%
Elevar Therapeutics regulatory FDA granted priority review to Elevar Therapeutics' NDA for lirafugratinib for pretreated cholangiocarcinoma, with a PDU… high 98%
Soficabtagene geleucel (WU-CART-007) regulatory FDA granted Breakthrough Therapy Designation to Soficabtagene geleucel (WU-CART-007) for relapsed or refractory T-cell l… high 98%
FDA announcement FDA Commissioner Marty Makary announced that speeding up drug approvals and increasing OTC drug availability are key age… medium 95%
trastuzumab deruxtecan regulatory FDA fast-tracked and granted priority review to trastuzumab deruxtecan for HER2-positive early breast cancer in March 20… high 98%
rusfertide regulatory FDA fast-tracked and granted priority review to rusfertide for polycythemia vera in March 2026. high 98%
lirafugratinib regulatory FDA fast-tracked and granted priority review to lirafugratinib for cholangiocarcinoma in March 2026. high 98%
luvesilocin regulatory FDA granted Breakthrough Therapy Designation to luvesilocin for postpartum depression (PPD). high 98%
milsaperidone regulatory FDA approved milsaperidone for schizophrenia and bipolar 1. high 98%
Avlayah regulatory FDA approved Avlayah for Hunter Syndrome in 2026. high 95%
Lifyorli regulatory FDA approved Lifyorli for platinum-resistant ovarian cancer in 2026. high 95%
Awiqli (insulin icodec-abae) regulatory FDA approved Awiqli (insulin icodec-abae) for type 2 diabetes in 2026. high 95%
Kresladi (marnetegragene autotemcel) regulatory FDA approved Kresladi (marnetegragene autotemcel) for severe Leukocyte Adhesion Deficiency-I in 2026. high 95%
Foundayo (orforglipron) regulatory FDA approved Foundayo (orforglipron) for weight loss in 2026. high 95%
Eli Lilly regulatory FDA approved Eli Lilly's Foundayo (orforglipron) for weight management under the National Priority Voucher program. high 98%
leucovorin regulatory FDA approved expanded use of leucovorin for cerebral folate transport deficiency in March 2026. medium 98%
tividenofusp alfa regulatory FDA granted accelerated approval to tividenofusp alfa for Hunter syndrome in March 2026. high 98%
Ionis Pharmaceuticals regulatory FDA accepted Ionis Pharmaceuticals' zilganersen NDA for priority review in Alexander disease in March 2026. high 98%
Capricor regulatory FDA lifted a complete response letter (CRL) for Capricor's deramiocel in March 2026. medium 98%
FORE Biotherapeutics regulatory FDA granted Breakthrough Therapy Designation to FORE Biotherapeutics' plixorafenib for BRAF V600E-mutated high-grade gli… high 95%
Praxis Precision Medicines regulatory Praxis Precision Medicines announced FDA acceptance and Priority Review of its NDA for relutrigine for SCN2A and SCN8A D… medium 95%
FDA announcement Amidst a turbulent year, the FDA is emphasizing efforts to speed up drug approvals through programs like the national pr… low 85%
Cogent Biosciences regulatory Cogent Biosciences submitted an NDA for bezuclastinib for Gastrointestinal Stromal Tumors (GIST) under the FDA's Real-Ti… medium 95%
BridgeBio Pharma regulatory BridgeBio Pharma submitted an NDA to the FDA for BBP-418 for limb-girdle muscular dystrophy type 2I/R9, potentially the … medium 95%
FDA announcement FDA Commissioner Marty Makary announced the agency's commitment to speeding up drug approvals and increasing over-the-co… low 90%
Egetis Therapeutics regulatory Egetis Therapeutics announced FDA acceptance and Priority Review of its NDA for Emcitate (tiratricol) for MCT8 deficienc… medium 95%
Fore Biotherapeutics regulatory FDA granted Breakthrough Therapy Designation to Fore Biotherapeutics' plixorafenib for adult patients with BRAF V600E–mu… medium 95%
Bristol Myers Squibb regulatory FDA accepted Bristol Myers Squibb's NDA for iberdomide for relapsed/refractory multiple myeloma, granting Breakthrough T… medium 95%
Eli Lilly regulatory Eli Lilly's orforglipron received a Commissioner's National Priority Voucher, expediting its review process prior to its… medium 85%
Orchard Therapeutics regulatory FDA granted accelerated approval to Orchard Therapeutics' Kresladi (marnetegragene autotemcel) for severe Leukocyte Adhe… high 95%
Eli Lilly regulatory FDA approved Eli Lilly's Foundayo (orforglipron) for obesity and weight-related conditions in a record 50 days under a p… high 100%
FDA regulatory FDA approved expanded use of leucovorin calcium tablets for cerebral folate transport deficiency, marking the first ther… medium 90%
Ionis Pharmaceuticals regulatory FDA accepted Ionis Pharmaceuticals' NDA for zilganersen for Alexander disease with priority review, setting a PDUFA date… medium 95%
WATCHER CONFIG
query: FDA drug approval NDA breakthrough therapy designation regulatory decision
event_types: ['regulatory', 'product', 'announcement']
impact_floor: all
time_window: 7
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FDA Drug Approvals
Medical · Updated Apr 04, 2026
ACTIVE
MONITORING OBJECTIVE
New drug approvals and regulatory decisions from the FDA. Includes NDA approvals, breakthrough therapy designations, and complete response letters.
NOTIFICATION FREQUENCY
Real-time notifications based on signal detection
SIGNAL METRICS
44
Total events
Apr 04
Last activity
DATA SCHEMA
Drug Name string
Company string
Indication string
Type string
Status string
Signal event details
FDA Drug Approvals
FIELD DATA
RAW DATA